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Most Frequently Encountered Inborn Errors of Metabolism
Book chapter

Most Frequently Encountered Inborn Errors of Metabolism

Jubara Alallah, Pankaj B. Agrawal, Alvaro Dendi and Akhil Maheshwari
Principles of Neonatology, pp.649-660
2023-01-01

Abstract

17-hydroxyprogesterone 2-methylcitrate tiglylglycine 21-hydroxylase 3-hydroxypropionate aciduria acyl carnitine acyl-CoA dehydrogenase medium chain gene adenosylcobalamin adrenocorticotropic hormone arginase argininosuccinate synthetase (ASS1) argininosuccinic aciduria argininosuccinic lyase argininosuccinic synthetase basal ganglia biochemical signature bradycardia branched-chain alpha-keto acid dehydrogenase branched-chain amino acids C3 acylcarnitine carbamoylphosphate synthetase I carglumic acid Casein glycomacropeptide citric acid cycle citrin deficiency citrulline coma CYP21A2 cytochrome P450 family 21 subfamily A member 2 protein developmental delay dihydrolipoyl dehydrogenase (E3)-deficiency Duarte variant edema encephalopathy enzyme Escherichia coli extracorporeal detoxification galactitol galactokinase galactose-1-phosphate uridylyltransferase galactosemia genetic glutamine high anion-gap metabolic acidosis homocystinuria type D protein hydrocortisone hyperammonemia hyperlactatemia hypothyroidism ketosis Krebs-Henseleit cycle lactose-containing feedings large neutral amino acids lethargy low-protein diet macroglossia maple syrup urine disease medium-chain acyl-CoA dehydrogenase medium-chain triglycerides metabolism metabolism of cobalamin associated A (MMAA) metabolism of cobalamin associated B (MMAB) methylmalonic aciduria methylmalonyl-CoA methylmalonyl-CoA mutase mitochondrial ornithine/citrulline antiporter mitochondrial (MMADH) Müllerian duct N-acetylglutamate synthase nonclassic adrenal hyperplasia or methylmalonic aciduria organic acidemias ornithine translocase orotic acid levels phenacetylglutamine phenylacetate phenylalanine phenylalanine hydroxylase phenylketonuria plasma amino acid analysis poor growth prolonged jaundice propionic acidemia propionyl CoA carboxylase propionyl-CoA carboxylase subunit alpha (PCCA) PCCΒ propionylcarnitine propionylglycine rare disorders respiratory alkalosis sapropterin dihydrochloride screening seizures short-chain fatty acyl-CoA SLC25A13 sodium benzoate soy-based formula tandem mass spectrometry tetrahydrobiopterin thyroglobulin TSH type 1 “classic/neonatal” citrullinemia type 2 citrullinemia umbilical hernia urea cycle urea cycle disorders uridine diphosphate galactose 4-epimerase (GALE) urinary orotic acid wide fontanelles

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