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Design of a Phase 3, Randomized, Placebo-controlled Trial of TofersenInitiated in Clinically Presymptomatic SOD1 Mutation Carriers with aLongitudinal Natural History Run-in
Journal article   Peer reviewed

Design of a Phase 3, Randomized, Placebo-controlled Trial of TofersenInitiated in Clinically Presymptomatic SOD1 Mutation Carriers with aLongitudinal Natural History Run-in

Michael Benatar
NEUROLOGY, Vol.96(15, S)
2021

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