Updates on Emerging Interventions for Autosomal Recessive ABCA4-Associated Stargardt Disease

Journal article

Peer reviewed

Liang Wang, Serena M. Shah, Simran Mangwani-Mordani and Ninel Z. Gregori

Journal of clinical medicine, Vol.12(19), p.6229

2023-09-27

PMID: 37834872

Abstract

ABCA4

adeno-associated viral vectors

deuterated vitamin A

emixustat

gene therapy

human embryonic stem cells

Stargardt disease

stem cell therapy

visual cycle modulators

url

https://doi.org/10.3390/jcm12196229View

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Title: Updates on Emerging Interventions for Autosomal Recessive ABCA4-Associated Stargardt Disease
Creators: Liang Wang - University of Miami
Serena M. Shah - University of Miami
Simran Mangwani-Mordani - University of Miami
Ninel Z. Gregori - University of Miami
Publication Details: Journal of clinical medicine, Vol.12(19), p.6229
Grant note: Bionic Vision Technologies
Academic Unit: UMMG Department of Ophthalmology; Miller School of Medicine
Language: English
Resource Type: Journal article
PMID: 37834872
Record Identifier: 991032796303802976